A single-center retrospective study reports durable immune recovery and high long-term survival after hematopoietic stem cell transplantation for a genetic combined immunodeficiency.
Key Takeaways
- Event-free survival were both 91.5% after a median seven years follow-up
- Matched related donor transplants had 94.6% survival and matched unrelated donors had 100% survival
- All survivors showed resolution of eczema and recurrent infections with robust immune reconstitution