News summary

BioMarin Announces Positive Results of Phase 3 VOXZOGO® (vosoritide) Study in Hypochondroplasia Published in NEJM Evidence

Source: PR Newswire • Published: 09 Sept 2026, 13:05

Summarized by Masters of Longevity from PR Newswire.

A news article summarizing published Phase 3 study results for a growth therapy in children with hypochondroplasia, outlining study design, measures evaluated, and clinical implications.

BioMarin Announces Positive Results of Phase 3 VOXZOGO® (vosoritide) Study in Hypochondroplasia Published in NEJM Evidence
Key Takeaways
  • Vosoritide treatment increased annualized growth velocity by an LS mean difference of 2.33 cm/year versus placebo.
  • Standing height, height Z-score, and arm span all improved significantly versus placebo after 52 weeks.
  • Safety profile matched prior achondroplasia studies with mostly mild adverse events and no treatment-related serious events.
Read the full article at PR Newswire

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